CAR T-cell therapy wins expert panel approval for leukemia treatment: What does this mean for myeloma patients?

On Wednesday, an advisory panel convened by the US Food and Drug Administration (FDA) voted 10 to 0 to recommend the approval of CAR T-cell therapy for treatment of children and young adults with late-stage leukemia. Novartis’s CTL019 is a gene-altering treatment directed against the protein CD19 found on the leukemic B-cells. Wednesday’s unanimous endorsement paves the way for the first gene therapy to win FDA approval, which is expected in September.